IPTACOPAN ASH UPDATE
Launch readiness to support rare disease success is on track
Patient engagement
and activation
Relationships built
with key patient
advocacy groups
■ Focus on educating PNH
patients on available
therapies and activating
them to seek treatment
that's right for their life
Disease state
education
Launched PNH disease
education campaign at
ASH 2022 to raise
awareness of high
burden of disease and
unmet need
Ongoing digital
engagement
Patient support
services
Detailed mapping of
patient journey to minimize
friction for new and switch
patients
Leveraging experience in
Rare Disease, Oncology
and MS to ensure best
practice
Comprehensive
evidence generation
Ph3 program covering
broad spectrum of PNH
patients: treatment naïve
(APPOINT) and switch
(APPLY)
Patient registries
with key stakeholder
organizations
Field medical and field sales teams already in place
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IPTACOPAN ASH UPDATE | DECEMBER 13, 2022
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