argenx SE Investor Day Presentation Deck slide image

argenx SE Investor Day Presentation Deck

Phase 1 Safety Results Support Proof of Concept Studies in Patients Any Grade 2 Grade 3 or higher Serious argenx ● ● 0.1 mg/kg ● 6 (75.0) 1 (12.5) 0.5 mg/kg 5 (62.5) 1 (12.5) 2.5 mg/kg Treatment-Emergent Adverse Events (TEAE) 5 (62.5) 1 (12.5) 1 (12.5) 10 mg/kg 5 (71.4) *Safety data still blinded in Phase 1 study 30 mg/kg 7 (100) 60 mg/kg 5 (62.5) 1 (12.5) TEAEs primarily Grade 1 and not dose-related Serious TEAE determined to be unrelated to drug No increased risk of infection N (%) 60 mg/kg SC 5 (62.5) 2 (25.0) 80 mg/kg 6 (75.0) 15 mg/kg SC 6 (75.0) 10-10-10-10 mg/kg 6 (75.0) 60-10-10 mg/kg Single and multiple administrations of ARGX-117 or placebo show favorable safety and tolerability profile to date* 8 (100) 10-50-20 mg/kg 8 (100) 15-15-15-15 mg/kg SC 8 (100) TEAE = treatment emergent adverse event n = number of subjects that experienced at least one TEAE % = number of subjects (n) as percentage Data Cut-off for Interim Analysis: May 20th 2021 57
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